One of the first lessons I learned in my career was that research study results often raise as many questions as they answer. Such is the case with new results from the gene therapy clinical trial for children and young adults with Leber congenital amaurosis (LCA, RPE65 mutations) at the Universities of Pennsylvania and Florida.
Posts tagged lca
Piggybacking on last week’s post by our CEO, Bill Schmidt, I wanted to tie two personal stories to exceptional advances made in retinal research in 2012. I’d be remiss if I didn’t mention that these advances were made possible by the generous support of FFB donors, and that future advances – which, eventually, will help 10 million Americans alone – depend on our donors’ continued support. I’ll revisit fundraising later in this post, but, first, you’ll find the first of the two stories – on how gene therapy restored some of a boy’s sight – below. The next story will be posted later this week.
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After a rigorous review process, the Foundation is funding eight new research projects for a wide range of conditions, including Leber congenital amaurosis (LCA), age-related macular degeneration (AMD) and retinitis pigmentosa (RP). You can read about these exciting projects in an article recently posted on the Foundation’s homepage.
It seems there is no dearth of fantastic cures being touted on the Internet and in email inboxes these days. Sort of reminds me of those old Western movies where the itinerant peddler sells the magic elixir that will cure any and all ailments you have. Continue Reading…
Imagine being born completely deaf or with profound hearing loss. Certainly, there are many challenges, but you find ways to navigate the hearing world. You learn sign language or get a cochlear implant. Through cultural and advocacy programs and education, you learn how to succeed in school, enjoy sports and social activities and plan for the future.
Steve is highly respected for his expertise and tireless commitment to finding treatments and cures for vision-robbing retinal diseases. 
As the Foundation's senior science writer, Ben writes science and research articles for the Foundation’s website, newsletters and Eye on the Cure blog. 
As the Foundation's senior writer, Rich writes and edits content for all of the Foundation’s print and online publications, including its blog, Eye on the Cure. 
Rockin’ and Rollin’ for a Good Cause
By Dr. Steve Rose on June 1, 2012 | 0 Comments
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